Enfermedad de Stargardt
A menudo diagnosticada en la niñez o adolescencia, la enfermedad de Stargardt es una forma hereditaria de degeneración macular que causa pérdida de visión central. La condición a veces es denominada degeneración macular juvenil o de arranque temprano.
Latest News
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ViGeneron Receives FDA Authorization to Launch Clinical Trial for mRNA Trans-splicing Gene Therapy for Stargardt Disease
Research NewsThe company is also planning to conduct the clinical trial at sites in the EU.
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SpliceBio Receives FDA Clearance to Launch Clinical Trial for Stargardt Disease Protein Splicing Therapy
Research NewsThe company has also launched a natural history study of patients to inform the planned clinical trial.
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Nanoscope Planning Phase 3 Clinical Trial of its Optogenetic Therapy for People with Advanced Stargardt Disease
Research NewsThe Phase 3 trial is expected to begin in Q1 2025
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Foundation Funds 25 New Grants Totaling $15.1 Million in FY23
Research NewsThe global leader in retinal degenerative disease research supports a total of 93 research grants in its portfolio.
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Foundation Commits More Than $15 Million to 23 Promising Research Projects for Eradicating Retinal Diseases
Research NewsFunding for the new grants was made possible by Foundation’s strong donor base and philanthropic partners
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Stargazer Pharmaceuticals Initiates a Phase 2a Clinical Trial for its Stargardt Disease Drug
In the PressThe Foundation Fighting Blindness Retinal Degeneration Fund is an investor in the company
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Foundation Fighting Blindness To Jointly Host Online Continuing Medical Education (CME, COPE) Webinar
Foundation NewsThe event will review best practices for care and management of patients with inherited retinal diseases such as retinitis pigmentosa, Usher syndrome, and Stargardt disease.
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Foundation Fighting Blindness Commits $6.5 Million for New Retinal Disease Research Grants
Foundation NewsNew grants include development of CRISPR/Cas9 gene-editing treatments, new disease models, and a retinal regeneration therapy
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COVID-19 Resources
Foundation NewsThe Foundation Fighting Blindness is closely monitoring the COVID-19 situation and its impact on the IRD community.
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ProQR Therapeutics Teams Up with the Foundation Fighting Blindness and Blueprint Genetics to Support the My Retina Tracker® Program for People Living with Inherited Retinal Diseases
Foundation NewsMy Retina Tracker Program is the highest volume IRD genetic testing program in the U.S.
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Blueprint Genetics, InformedDNA and the Foundation Fighting Blindness launch an open access program for patients with inherited retinal disease in the United States
Foundation NewsThe program will offer patients with inherited retinal disease no-cost genetic testing and genetic counseling in the United States. Look for updated information on how to participate to be posted in mid-October, with program registration starting shortly thereafter.
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Foundation Fighting Blindness Investing Nearly $6.5 Million in New Grants
Foundation NewsThe newly funded research efforts include several therapies that have strong potential to treat a wide range of inherited retinal diseases.
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Foundation Fighting Blindness Endorses 'Eye Bonds' Legislation
Foundation NewsBipartisan Bill Will Stimulate Up to $1 Billion in New Funding for Blindness Research
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Foundation Fighting Blindness Urges Congress to Pass ‘Eye-Bonds’ Legislation
Foundation NewsBill Introduced in U.S. House Would Speed Up Cures for Blindness
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Foundation Fighting Blindness Clinical Research Institute Hosted Workshop for ProgStar, the Largest Natural History Study for Stargardt Disease Ever Launched
Foundation NewsThe primary goal of the landmark study, funded by the Foundation, is to provide companies and researchers with disease-progression data and potential clinical trial endpoints to drive therapy development
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Foundation Fighting Blindness and CheckedUp® Partner to Educate Retinal-Disease Patients About Research, Resources, and Emerging Therapies During Doctor Visits
Foundation NewsThe Foundation Fighting Blindness (the Foundation) and CheckedUp have formed a collaborative partnership to deliver patient-friendly diagnostic and disease-management information to people with retinal diseases such as age-related macular degeneration, retinitis pigmentosa, and Stargardt disease during their visits to eye doctors.
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Researchers Take another Critical Step toward Using Skin Cells to Treat Retinal Disease
Foundation NewsA research team funded by the Foundation Fighting Blindness used an innovative repair technique to correct the disease-causing genetic defect in stem cells derived from a person’s skin — stem cells that hold the potential to treat their retinal degenerative condition.
Podcasts
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Eye on the Cure Podcast | Episode 80: Aniz Girach, MD
Eye on the CureAniz Girach talks about the company’s emerging protein-splicing therapy for Stargardt disease which has received clearance from the FDA to move into a clinical trial.
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Eye on the Cure Podcast | Episode 77: Dr. Bob Bell
Eye on the CureDr. Bell, the CSO of Ascidian Therapeutics, talks about STELLAR, the company’s Phase ½ clinical trial for its emerging RNA-rewriting therapy for Stargardt disease (ABCA4 mutations).
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Eye on the Cure Podcast | Episode 71: Dr. Leonide Saad
Eye on the CureDr. Saad discusses an emerging therapy for Stargardt disease that has performed well in clinical trials.
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