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Displaying 521–530 of 866 results for “vision connection”
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Foundation Joins the Institute for Gene Therapies, a Newly Formed Advocacy Organization
Research NewsIGT to accelerate gene therapy development and patient access
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AGTC Reports Positive Six-Month Results for XLRP Phase 1/2 Gene Therapy Trial
Research NewsThe company is planning a Phase 3, pivotal trial for end of 2020
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Ashlyn Experiences Joy in Day-To-Day Life After Sight Is Restored
Beacon StoriesAshlyn’s vision was restored following her treatment with the LUXTURNA gene therapy.
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FDA Authorizes Stem Cell Clinical Trial for RP in Los Angeles
Research NewsPhase 1/2a human study will evaluate neural progenitors for preserving vision
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Beacon Stories
13 year old Kailey Reichardt’s personal essay about her little sister Ashlyn, who was diagnosed with Leber congenital amarosis (LCA) at a young age. Kailey is a Beacon for other siblings impacted and going through similar situations.
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The Retina is a Proving Ground for a Broad Range of Neurological Therapies
Research NewsRetinal research paves the way for new treatments for the entire neurological system.
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Information for affected individuals and their families about the role of genetic counseling.
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First Patient Receives ProQR’s Emerging USH2A Therapy in Clinical Trial
Research NewsProQR, a developer of RNA therapies in the Netherlands, announced that the first clinical-trial participant has received its emerging treatment, which targets retinitis pigmentosa and Usher syndrome caused by mutations in exon 13 of the USH2A gene.
