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Displaying 1–10 of 387 news results
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Jul 6, 2026
Belite Bio Submits New Drug Application to FDA for its Stargardt Treatment
Research NewsTinlarebant becomes first Stargardt treatment submitted to FDA for approval
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Jun 18, 2026
Potential Oral Stargardt Treatment Advances to Phase 3 Clinical Trial
Research NewsPromising oral treatment moves closer for Stargardt patients.
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May 11, 2026
Research News2020 Llura Liggett Gund Award recipient honored for pioneering gene therapy that transformed vision research.
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Apr 21, 2026
Atsena Therapeutics Advances to Pivotal Phase 3 Trial for X-Linked Retinoschisis
Research NewsData monitoring committee recommends proceeding with registration-enabling study for ATSN-201
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Apr 16, 2026
MeiraGTx Acquires XLRP Gene Therapy Bota-Vec, Moves Toward Regulatory Filing
Research NewsMeiraGTx has acquired bota-vec, a gene therapy for X-linked retinitis pigmentosa (XLRP), and plans to file for regulatory approval in the U.S., Europe, and Japan, with a potential launch in 2027.
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Apr 14, 2026
Age-Related Macular Degeneration Research Advances
Research NewsRecent developments in research on age-related macular degeneration.
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Apr 14, 2026
Usher Syndrome Research Advances
Research NewsRecent developments in research on Usher Syndrome.
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Apr 14, 2026
Stargardt Disease Research Advances
Research NewsRecent developments in research on Stargardt disease.
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Apr 14, 2026
Leber Congenital Amaurosis Research Advances
Research NewsRecent developments in research on Leber congenital amaurosis.
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Apr 14, 2026
Retinitis Pigmentosa Research Advances
Research NewsRecent developments in research on retinitis pigmentosa.