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Displaying 71–80 of 242 diseases results
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Jan 24, 2025
Eye on the Cure Podcast | Episode 80: Aniz Girach, MD
Eye on the CureAniz Girach talks about the company’s emerging protein-splicing therapy for Stargardt disease which has received clearance from the FDA to move into a clinical trial.
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Jan 10, 2025
Atsena to Launch Part B of Phase 1/2 Clinical Trial for XLRS Gene Therapy
Research NewsThe Foundation is a founding investor in Atsena.
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Jan 10, 2025
Eye on the Cure Podcast | Episode 79: Damon Lembi
Eye on the CureDamon Lembi talks about his journey as a college baseball star, father, and CEO of Learnit.
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Dec 20, 2024
Research NewsThe company is also planning to conduct the clinical trial at sites in the EU.
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Dec 20, 2024
Eye on the Cure Podcast | Episode 78: Dr. Sheldon Rowan
Eye on the CureDr. Rowan talks about the impact of the glycemic index, microbiome, and diet on the development of age-related macular degeneration and optimization of overall retinal health.
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Dec 16, 2024
Research NewsThe company has also launched a natural history study of patients to inform the planned clinical trial.
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Dec 16, 2024
Staying True to Music, Family, and Advocacy
Beacon StoriesMusic duo Andrew & Polly have earned a GRAMMY nomination for their children’s album “Ahhhhh!” while also championing disability awareness and inclusivity. Andrew’s experience with Stargardt disease fuels their advocacy, inspiring others through their music, podcast, and dedication to research and community support.
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Dec 13, 2024
Sepul Bio Launches Phase 2b Clinical Trial for USH2A RNA Therapy
Research NewsKnown as ultevursen, the USH2A RNA therapy was licensed from ProQR.
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Dec 6, 2024
Eye on the Cure Podcast | Episode 77: Dr. Bob Bell
Eye on the CureDr. Bell, the CSO of Ascidian Therapeutics, talks about STELLAR, the company’s Phase ½ clinical trial for its emerging RNA-rewriting therapy for Stargardt disease (ABCA4 mutations).
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Nov 15, 2024
Eye on the Cure Podcast | Episode 76: The Lemay-Pelletier Family
Eye on the CureWhen the Lemay-Pelletier family from Montreal learned that three of their four children were losing vision from retinitis pigmentosa, they made the bold decision to spend 15 months traveling the world to give their kids as many visual memories as possible.