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Displaying 351–360 of 651 for “retinal diseases”
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AGTC Announces Development of Stargardt Disease Gene Therapy
Research NewsDual-vector delivery system designed to deliver the large ABCA4 gene
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First Patient Receives ProQR’s Emerging USH2A Therapy in Clinical Trial
Research NewsProQR, a developer of RNA therapies in the Netherlands, announced that the first clinical-trial participant has received its emerging treatment, which targets retinitis pigmentosa and Usher syndrome caused by mutations in exon 13 of the USH2A gene.
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Clinical Trial Authorized in the U.S. for Emerging LCA 10 Therapy
Research NewsProQR, a biotechnology company in the Netherlands, has received authorization from the U.S. Food and Drug Administration to start a Phase I/II clinical trial for its therapy known as QR-110
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First Patient Treated in XLRP Gene Therapy Clinical Trial
Research NewsThe Nightstar gene therapy involves injection of healthy copies of RPGR underneath the retina.
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A Surprising Number of Carrier Females are Affected by X-Linked Retinitis Pigmentosa
Research News40 percent of genetically tested XLRP carriers showed a definitive abnormality in at least one of three visions tests.
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Taking Their Story of Vision Loss on the Road
Beacon StoriesRollie and Sandie Purvis, parents of two sons with choroideremia, describe their sons’ film project, “Driving Blind.”
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Sepul Bio’s LCA10 RNA Therapy Moves into Phase 3 Clinical Trial
Research NewsThe emerging therapy improved vision for some participants in an earlier clinical trial.
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Research News
Durable vision improvements were also observed out to 18 months for previously dosed adult patients in the trial.
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Eye on the Cure Podcast | Episode 91: Dr. George Magrath
Eye on the CureDr. George Magrath is the CEO of Opus Genetics, a clinical-stage biopharmaceutical company developing gene and small molecule therapies for vision-threatening eye diseases.
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Turning RP into a Canvas of Hope
Beacon StoriesDiagnosed with retinitis pigmentosa (RP) at 12, Raquel spent years navigating vision loss without support. But everything changed when she connected with the Foundation Fighting Blindness — and found not just answers, but community. Now an artist, advocate, and leader in San Diego, Raquel uses her story and her art as the founder of Unblurred Collection to raise awareness, give back, and inspire others living with blinding diseases.
