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Displaying 111–120 of 705 for “retinitis clinical trial”
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Twelve People Receive XLRS Gene Therapy in AGTC's Clinical Trial
Research NewsAGTC’s gene therapy uses a human-engineered virus — and adeno-associated virus or AAV — to deliver normal copies of retinoschisin to the patient’s retina.
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ARVO 2016: Choroideremia Gene Therapy in Clinical Trial Continues to Perform Well
Research NewsFive of six patients in NightStaRx’s choroideremia gene-therapy trial continue to benefit from the treatment.
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Opus Genetics Receives FDA Clearance to Launch Clinical Trial for Best1 Gene Therapy
Research NewsThe Foundation funded earlier, proof-of-concept studies for the Best1 gene therapy and later launched Opus to develop several IRD gene therapies.
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Neurogene to Launch Gene Therapy Clinical Trial for Children with Batten Disease
Research NewsThe treatment will be delivered to the vitreous of the eye and ventricles of the brain
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Research News
The emerging treatment targets a specific mutation (c.2991+1655A>G in Intron 26) of the gene CEP290 which causes Leber congenital amaurosis 10 (LCA 10)
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Atsena to Launch Part B of Phase 1/2 Clinical Trial for XLRS Gene Therapy
Research NewsThe Foundation is a founding investor in Atsena.
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FFB-CRI Leads Effort to Identify Outcome Measures for Therapies in Clinical Trials
Research NewsImproved outcome measures will make clinical trials for degenerative retinal diseases — including age-related macular degeneration (AMD), the world’s leading cause of blindness in seniors, and inherited retinal conditions such as RP and Stargardt disease — less expensive to conduct and able to deliver more precise results.
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Stem-Cell Therapy for Retinitis Pigmentosa Safe Thus Far in Early Human Study
Research NewsThe trial is one of the first-ever for a stem-cell-derived therapy for RP.
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Vision Testing and Retinal Imaging in Clinical Trials: What Patients Can Expect
Research NewsBecause measuring changes is not always easy, people in clinical trials often undergo a number of different tests over one or several years. It can be challenging for the patient, but is necessary to determine if a treatment is working.
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Best Disease Gene Therapy Advances Toward Clinical Trial
Research NewsUsing gene therapy, FFB-funded researchers at the University of Pennsylvania School of Veterinary Medicine (Penn Vet) and Perelman School of Medicine have reversed the disease process in a canine model of Best disease, an inherited form of macular degeneration that can lead to severe vision loss in humans
