
Transcripts and Audio Recordings from the 2019 Investing in Cures Summit, held at The Umstead Hotel & Spa in Cary, North Carolina on March 2, 2019
Transcripts
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Welcome & Opening Remarks
Inherited Retinal Disease Science Landscape
Brian Mansfield, PhD, Foundation Fighting Blindness
Inherited Retinal Disease Science Updates Panel
Moderated by Stephen Rose, PhD, Foundation Fighting Blindness
• Leah Byrne, PhD, University of Pittsburgh
• Joseph Carroll, PhD, The Medical College of Wisconsin
• Trevor McGill, PhD, Oregon Health & Science University
• Eric Pierce, MD, PhD, Massachusetts Eye & Ear
The Art of Translation Panel
Moderated by Amy Laster, PhD, Foundation Fighting Blindness
Retinal Degeneration Fund Portfolio & Emerging Company Updates
Moderated by Ben Yerxa, PhD, Foundation Fighting Blindness
• HORAMA: Christine Placet
• Mireca: Prof. François Paquet-Durand
• Nacuity Pharmaceuticals: Halden Conner
• Nayan Therapeutics: Milind Desphande, PhD
• ProQR: David Rodman, MD
• SparingVision: Stephen Rose, PhD
Summit Luncheon
featuring keynote speaker
Omid Karkouti, MS
Co-Founder & CEO, Perception Therapeutics
Public Company Forum
Moderated by Rusty Kelley, PhD, MBA • Foundation Fighting Blindness
• AGTC: Sue Washer
• Eloxx Pharmaceuticals, Inc: Robert Ward
• miRagen Therapeutics: William Marshall, PhD
• Nightstar Therapeutics: David Fellows
• Ophthotech: Kourous Rezaei, MD
Public Company Forum Q&A
The Ecosystem Panel
Moderated by Kelly Lisbakken, Wedbush Securities
• John Corneille, JD, Foundation Fighting Blindness
• Mark McClellan, MD, PhD, Duke University
• David Nierengarten, PhD, Wedbush Securities
• Eric Pierce, MD, PhD, Massachusetts Eye & Ear
• Christy Shaffer, PhD, Hatteras Venture Partners
• Kali Stasi, MD, PhD, Novartis
• Sue Washer, AGTC
Closing Remarks
Warren Thaler, MBA
Chairman, RD Fund