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Displaying 41–50 of 285 research results
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Eye On the Cure Research News
Survey results will inform therapy developers and the agenda for a Patient-Focused Drug Development meeting with Food and Drug Administration representatives.
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Eye On the Cure Research News
The company is currently developing programs for Stargardt disease (ABCA4), Usher syndrome, RP25 (EYS), and RP1.
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ProQR Doses First Patients in Phase 2/3 Clinical Trials for its USH2A-Exon 13 RNA Therapy
Eye On the Cure Research NewsThe Sirius trial is for USH2A (exon 13 mutations) patients with advanced vision loss. The Celeste trial is for USH2A (exon 13 mutations) patients with moderate to early vision loss.
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Ocugen to Launch Clinical Trial for Cross-Cutting RP Gene Therapy
Eye On the Cure Research NewsThe clinical trial is for RHO and NR2E3 mutations, but the retinal gene therapy has the potential to benefit people with a variety of other mutated genes
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Geographic Atrophy: The Advanced Form of Dry AMD
Science EducationGeographic atrophy causes significant central vision loss and remains an unmet medical need.
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FDA Approves Genentech’s Susvimo for Treating Wet AMD
Eye On the Cure Research NewsThe approach significantly reduces the need for regular ocular injections.
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Atsena Therapeutics Developing X-Linked Retinoschisis Gene Therapy
Eye On the Cure Research NewsThe emerging gene therapy is being designed to more safely reach the fovea
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Foundation Hosts Workshop on USH1B Research and Therapy Development
Eye On the Cure Research NewsEmerging dual-vector gene therapies to address current cargo-size limitations were highlighted during the meeting.
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Eye On the Cure Research News
The emerging treatment targets a specific mutation (c.2991+1655A>G in Intron 26) of the gene CEP290 which causes Leber congenital amaurosis 10 (LCA 10)
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RD Fund Launches Opus Genetics to Advance Gene Therapies for Inherited Retinal Diseases
Eye On the Cure Research NewsFirst two programs are for Leber congenital amaurosis: LCA5-lebercillin and LCA13-RDH12
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