
Research News
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ARVO 2025 Highlight: J&J’s XLRP Gene Therapy Didn’t Meet Primary Endpoint in Phase 3 Clinical Trial
Despite missing the primary endpoint, the treatment improved vision for some patients.
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The company is planning a Phase 2/3 clinical trial for the therapy in late 2025.
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Part B of the trial will enroll nine adult patients as well as three pediatric patients.
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The company is currently enrolling patients in its Phase 2/3 VISTA Clinical Trial.
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Retinitis Pigmentosa Research Advances
Recent developments in research on retinitis pigmentosa.
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Stargardt Disease Research Advances
Recent developments in research on Stargardt disease
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Leber Congenital Amaurosis Research Advances
Recent developments in research on Leber congenital amaurosis
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Age-Related Macular Degeneration Research Advances
Recent developments in research on age-related macular degeneration.
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Atsena Receives $150 Million in New Financing to Advance XLRS and Preclinical Gene Therapy Programs
The company has reported encouraging results from its LCA1 and XLRS gene therapy clinical trials.