Research News
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Belite Bio to Seek FDA Approval for its Stargardt Disease Drug
Research NewsTinlarebant slowed disease progression by 36 percent in the Dragon Phase 3 clinical trial.
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Opus Genetics Launches Gene Therapy Clinical Trial for Best Disease
Research NewsThe Foundation funded preclinical studies for the approach and launched Opus.
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SparingVision Launches Clinical Trial for Therapy to Re-Activate Dormant Cones in Advanced RP
Research NewsThe approach may provide better visual acuity than current optogenetic therapies in clinical trials.
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Retinitis Pigmentosa Research Advances
Research NewsRecent developments in research on retinitis pigmentosa.
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Leber Congenital Amaurosis Research Advances
Research NewsRecent developments in research on Leber congenital amaurosis.
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Stargardt Disease Research Advances
Research NewsRecent developments in research on Stargardt disease.
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Age-Related Macular Degeneration Research Advances
Research NewsRecent developments in research on age-related macular degeneration.
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Annual Funded Grants – CRISPR and Prime Editing Technologies
Research NewsFunded grants for CRISPR and prime editing approaches.
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Sepul Bio’s LCA10 RNA Therapy Moves into Phase 3 Clinical Trial
Research NewsThe emerging therapy improved vision for some participants in an earlier clinical trial.