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Displaying 1–10 of 395 diseases results
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Apr 25, 2024
We’re honoring National DNA Day with the Danny family!
When Sarah and A. J. found out their oldest daughter Lucia had Stargardt disease, it was a challenge to process her diagnosis. And when they connected with the Foundation, they realized their other five children could also be affected. Through the Foundation’s My Retina Tracker® Genetic Testing Program, they learned their five-year-old daughter Sarafina also has Stargardt disease. Now, Lucia and Sarafina have a bond like no other, and call each other the “Stargardt Sisters.”
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Apr 19, 2024
SalioGen Developing Novel Gene Insertion Therapy for Stargardt Disease
The company’s innovative Gene Coding™ platform enables seamless insertion of DNA into selective genomic locations.
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Apr 16, 2024
Eye on the Cure Podcast | Episode 64: Dr. Kapil Bharti
Kapil Bharti, PhD, a senior investigator and director of the Intramural Research Program at the National Eye Institute (NEI), talks with host Ben Shaberman about his clinical trial underway for an innovative cell therapy for geographic atrophy (advanced dry age-related macular degeneration) as well as a clinical trial of the drug metformin for Stargardt disease.
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Apr 12, 2024
Phase 3 Clinical Trial of NAC Launched for RP Patients
The drug is thought to work independent of the mutated gene causing RP.
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Apr 11, 2024
ViGeneron Launches Clinical Trial of Gene Therapy for RP Caused by CNGA1 Mutations
The gene therapy is administered using a less-invasive intravitreal injection.
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Apr 8, 2024
Ocugen to Launch Phase 3 Clinical Trial of Modifier Gene Therapy for RP
The emerging treatment is designed to work independent of the patient’s mutated gene.
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Apr 8, 2024
What Does “Blindness” Really Mean?
Jenny Schisler has retinitis pigmentosa. Jenny wants to spread awareness of what having a visual impairment really means to her and others affected by retinal degenerative diseases.
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Mar 27, 2024
Nanoscope Plans to Apply for FDA Approval for its Optogenetic Therapy
The company reported positive two-year results for its Phase 2 clinical trial of MCO-010.
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Mar 26, 2024
Opus Reports Vision Improvements for Patients in LCA5 Gene Therapy Clinical Trial
The company plans to administer a higher dose of the emerging gene therapy to the next group of patients.
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Mar 25, 2024
Collaboration will add a new multi-gene cohort of patients living with inherited retinal diseases. Data insights from the new study cohort will inform the future clinical trial design for BlueRock’s pipeline of cell therapies for treating blindness.